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PTCy-based allo-BMT platform as a curative, accessible alternative for pediatric and young adult severe aplastic anemia.

Authors: Dionysiou M, Ktena YP, Bonifant CL, Chen AR, Llosa NJ, Zambidis ET, DeZern AE, Jones RJ, Symons HJ, Cooke KR
Journal: Blood advances
family therapy mental health open access

Abstract